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Publication
PropertyValue
Working Groups RG Fischer, RG Gärtner
SubprojectNone
Open AccessOpen Access Yes
Publication TypeCongresses
Peer ReviewedUnknown
DOIDOI 10.1055/s-0043-1777171
Publication Year2023
TitleTazarotene and Bexarotene Show Efficacy as In Vitro Therapeutic Agents in Multiple Sulfatase Deficiency
JournalNeuropediatrics
ISSN0174-304X
eISSN1439-1899
URL https://www.thieme-connect.com/products/ejournals/html/10.1055/s-0043-1777171#info
PagesS1-S32
IssueS 01
Volume54
Journal AbbreviationNeuropediatrics
AuthorsSchlotawa L, Matysiak K, Kettwig M, Ahrens-Nicklas RC, Baud M, Berulava T, Brunetti-Pierri N, Gagne A, Herbst ZM, Maguire JA, Monfregola J, Pena T, Radhakrishnan K, Schröder S, Waxman EA, Ballabio A, Dierks T, Fischer A, French DL, Gelb MH, Gärtner J
First AuthorSchlotawa L
Last AuthorGärtner J

 External Resources

 272200  OMIM identifier (272200, Multiple Sulfatase Deficiency; MSD)

 0000-0002-7415-4905  ORCID identifier (Lars Schlotawa)

 0000-0003-4804-7716  ORCID identifier (Matthias Kettwig)

 0000-0002-9329-8912  ORCID identifier (Tonatiuh Pena Centeno)

 0000-0003-4562-7969  ORCID identifier (Elisa A. Waxman)

 0000-0001-8546-1161  ORCID identifier (André Fischer)

 0000-0003-4108-7109  ORCID identifier (Jutta Gärtner)

 02pttbw34  ROR identifier (02pttbw34, Baylor College of Medicine)

 02hpadn98  ROR identifier (02hpadn98, Bielefeld University)

 01z7r7q48  ROR identifier (01z7r7q48, Children's Hospital of Philadelphia)

 043j0f473  ROR identifier (043j0f473, German Center for Neurodegenerative Diseases)

 05xy1nn52  ROR identifier (05xy1nn52, Multiscale Bioimaging)

 04xfdsg27  ROR identifier (04xfdsg27, Telethon Institute Of Genetics And Medicine)

 021ft0n22  ROR identifier (021ft0n22, University Medical Center Göttingen)

 05290cv24  ROR identifier (05290cv24, University of Naples Federico II)

 01ryk1543  ROR identifier (01ryk1543, University of Southampton)

 00cvxb145  ROR identifier (00cvxb145, University of Washington)

 mbexc.de...iency/  Website entry (mbexc.de)

 mbexc.de...iency/  Website entry (mbexc.de)